I can understand that feeling of having butterflies in the stomach. The long delay only makes it worse (whatever be the reason)
For now, we can hope for the best; that the Rett results will be really good and robust enough (replicated) in adults, while being stellar in kids, given their age.
Let the results tell the story starting with Top Line Data
Fair enough, and I appreciate the reply. Personally, I tend to view the significant funding to be a rather prudent and timely move when facing the potential of a solo rare disease drug launch, but of course I can see how it could be viewed/utilized otherwise. I have no qualms with your 3 scenaris post, and appreciate maintaining a level approach. Cheers.