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jq1234

02/12/13 4:46 PM

#156885 RE: biotech jim #156882

I don't disagree with 6MWT driving approval. I am only talking about accelerated approval filing. Let's do one step at time. If filing allowed, I expect additional 6MWT data from trial extension are needed. The kids in the trial are approaching 12-13 years old, their continued stabilization of 6MWT would play important role in approval decision due to natural disease history alone.

I would be interested to see similar dystrophin data if eteplirsen is giving to those non exon 51 skipping DMD patients.