Biotech Values

[biotech jim]

The data on muscle fiber expression of dystrophin is nice, but based on my past (direct experience) and current view of the agency, the 6 MWT will drive approval. Need more patient data and also longer time frame for treatment to determine whether the increased expression translates to function.

I would like to rigorously analyze their cellular expression data, as these types of "quantitative" studies are not always so.