Genzyme of course is the leader and should dominate the arena. Other big players are Shire, Biomarin and Alexion. Lysosomal storage disorders (at least 40 have been identified) are a major class for ERTs. They are divided into several categories. These include the glycosphingolipidoses, such as Gaucher and Fabry diseases, and the mucopolysaccharidoses (MPSs), including MPS I-VII and their various subtypes. For many there is no treatment yet. For further reading:
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