Biotech Values

[genisi]

Genzyme of course is the leader and should dominate the arena. Other big players are Shire, Biomarin and Alexion.
Lysosomal storage disorders (at least 40 have been identified) are a major class for ERTs. They are divided into several categories. These include the glycosphingolipidoses, such as Gaucher and Fabry diseases, and the mucopolysaccharidoses (MPSs), including MPS I-VII and their various subtypes. For many there is no treatment yet.
For further reading:

http://www.lysosomallearning.com/healthcare/about/lsd_hc_abt_lsd.asp