News Focus
News Focus
icon url

Doc328

10/25/21 12:42 PM

#333722 RE: sokol #333720

Gene therapy has to be administered very early in life to prevent most of the changes. As a gene deletion disease, Rett does seem perfectfor this type of therapy. We are many years out from knowing what is best and hopefully a drug will be shown to make a real difference in a Rett girl's life and family. .