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News Focus
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boi568

10/25/21 9:04 AM

#333704 RE: frrol #333703

It sounded like she was excited because she had reason to be excited as someone who has been running an Anavex EXCELLENCE clinical trial. And strong signals that something good is happening in that trial would also tend to raise hopes that even a cure is possible with gene editing.

It takes a bit of an effort to discount these remarks to nothing more than generalized enthusiasm; researchers are like everyone else, they can be excited or discouraged, happy or sad. Every 2-73 investigator we hear about seems to be at the far end of excited and optimistic. Perhaps it is more than coincidence.
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Doc328

10/25/21 10:40 AM

#333715 RE: frrol #333703

Gene therapy for Rett may be around the corner. Novartis is trying to get an IND for OAV201, a gene therapy for Rett. I imagine the IND process for gene therapy is more complicated than for a small molecule.

Some news from the Rett Syndrome Research Trust. . They seem excited.

Also another gene therapy is also in the works. The Rett Society of Australia seems very excited.