Steadyt I didn’t get to listen to the presentation however, there are 2 other rare disorders that were referenced in the recently issued new patent 11/30/2020: Williams Syndrome and Smith-Magenis Syndrome. See examples 6 & 7. One of these could be the yet-to-be-announced indication for another new trial in 2021:
“Example 6
Williams Syndrome--Weight Gain
[0062] A 2 year-old male presents with Williams syndrome. He exhibits a failure to thrive with low weight gain. He begins treatment with i.v. doses of A2-73 at 5 mg every other day. After 60 days of treatment, he exhibits a 10% weight gain.
Example 7
Smith-Magenis Syndrome--Sleep
[0063] A 5 year-old male presents with Smith-Magenis syndrome. He experiences disturbed sleep. He begins treatment with oral doses of A2-73 at 10 mg/day. After 15 days of treatment, his sleep is markedly less disturbed.”