World Orphan Drug Congress USA 2018 - Conference Day One @ 11:25
Empowered educated patients influencing pre-clinical development and working with industry to optimize drug discovery
Patient groups role guiding research, disease understanding, supporting pre-clinical development and follow up experiments
Driving translational research and the influence on formulation, routes to delivery and overall clinical development
Effective partnerships between advocacy and industry to expand collaborations that can support enrollment and physician engagement
Christopher Missling, President and CEO, Anavex Life Sciences
Steven Kaminsky, Chief Science Officer, International Rett Syndrome Foundation