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Replies to #68744 on Biotech Values
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ghmm

11/19/08 4:09 PM

#68745 RE: ghmm #68744

Forgot about the CNS involvement for Hurler-Scheie
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genisi

11/19/08 4:12 PM

#68746 RE: ghmm #68744

More than a half of the patients with MPS-I opt for BMT and that leaves less for ERT. BMT is recommended for example, for all Hurler’s patients under the age of 2 years old.
I think the 1-169,000 prevalence refers to MPS-IVa alone.
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genisi

11/19/08 4:36 PM

#68748 RE: ghmm #68744

Sorry M, the 1/300,000 refers to MPS VI prevalence not IV.
(Guess I've passed my sleeping hour)