Thursday, May 12, 2011 1:35:06 PM
1-Pompe basically done dosing the 1st dose weight 4-6 weeks and go on to second cohort. No AE's. Think end of the year would be at third (20mg) cohort.
2-It seems the company is already exploring the possibility of a 3rd manufacturing plant. It would be outside the US for tax reasons and from what JJ was saying they may have even priced a couple as he said they are selling a discounts to what it would cost to build. Think around 2016 (2nd year of GALNS if everything goes well) would need one.
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