Nice find thanks! I don't see what is being done in cohort C (vs b & d).
to be off topic a little I saw a poster about Naglazyme A Follow-Up of Enzyme Replacement Therapy in Two MPS VI Patients with Poorly Engrafted Bone Marrow Transplantation. I thought BMT was not an option for MPS VI. A little more research and I found it is an option in some do you know how common? Am I right in thinking BMT is not an option in Morquio too. TIA!