I haven't bought a pure GT company if I do any time soon it may be QURE. I like that they are focusing internally on rare diseases.
I am still cautious about long term consequences but in (some) rare diseases there may be a bit more room especially if greater efficacy is obtainable.
My other main concern (From an investment standpoint great for patients though) is that I'm not sure how high a hurdle to entry gene therapy is. Granted some may be better than others but it seems every couple days we hear about some university program being licensed.
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