It depends on the specific disease. The “desperation” for a treatment from the patients and families generally determines the “standard” or “threshold” of the evidence of benefit. ALS is a devastating disease without any “effective” treatment at all. The drug from Amylyx shows likely benefit. The approval is warranted in my opinion. Hope better options will be available soon.
so it goes with Big government AZZholes !!!!!! Don't know WTF they are doing !!!!!!!
Don't look now, but such would be consistent w/what we have these days. Politics and Medicine should not be mixed but (today) we have evidence of exactly that.
I do not foresee AVXL lowering the bar. However, after decades of zero CNS med. progress maybe the "system" have decided to reset the bar so they could point to it and claim a medical victory . Standby, B/C that is the kind of zero .."RESET", that could happen. Note: very much like what just happened w/the BIIB -AD PR.
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