Has it really taken 2 months to let us know if the primary endpoint was met on 31 patients? Missling has stated that they present data at scientific conferences. There have been a number of Rett and rare disease conferences since the data was available to the company. There is only one more rare disease conference left this year that is a big enough to make an appearance. https://www.orphandrugsus.com/ Their program doesn't have anything about specific diseases but more about rare diseases in general.
In my opinion there are three reasons we haven't seen the results.
1) Like PDD they haven't met the primary endpoints and are taking their time to make that call. As long as they still are unsure (it isn't material yet) 2) Haven't liked their conference choices (not likely imo) 3) Filed for approval and wants to present approval and data at the same time.
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