blue,
US approval vs Aus approval for Rett: more info to come. Spoke w FDA representative regarding the RPD.
Bet on US, my opinion.
Agree - news can hit any time. These guidances are the green light, along with our FDA priority review.
Additional fyi: Rare Disease Day is end of Feb. This year it falls on Leap Day Feb 29, 2020. Our completion date for Rett (estimate): Mar 30, 2020.
We Got This!
Bio