Replies to post #165454 on Biotech Values

[drbio45]

Six minute walk is a rediculous way to measure benefit in the disease

proof of that is the two children that became non ambulatory even though their dystrophin levels increased

They can't walk but they aren't entering the olympics. They die of heart failure because their heart muscle dies. Chances are the increased dystrophin will allow them to live longer, but I guess they are no longer on the drug so they will die.