ACT TREATMENT GRANTED ORPHAN DRUG STATUS! fwiw, that happened over a year ago.. June 27, 2011 ACT Granted EU Orphan Medicinal Product Designation for hESC-Derived RPE Cells for Treatment of Stargardt's Disease http://www.advancedcell.com/news-and-media/press-releases/act_granted_eu_orphan_medicinal_product_designation_for_hesc-derived_rpe_cells_for_treatment_of_stargardts_disease/index.asp