Amicus Therapeutics, Inc. (FOLD)

[Glider549]

Amicus was able to achieve positive interim results from a phase 1/2 study using AAV-CLN6 gene therapy to treat patients with Batten disease.

Another gene therapy, known as AT-GAA, is currently being explored in a phase 3 study to treat patients with Pompe disease; enrollment completion is expected end of 2019.

The 6-month and 24-month data using AT-GAA to treat patients with Pompe disease are expected to be presented at the World Muscle Society October 1-5, 2019.

Amicus Therapeutics had $575.7 million in cash as of June 30, 2019, with enough cash to fund its operations into 2021.