Biotech Values

[ghmm]

I don't think its that simple the FDA is guilty of being too involved with the patient families. I don't recall that ever being done before. Janet Woodcock in particular probably said too much. BTW Adan Feuerstein tweeted that she will be in attendance at the adcom. At 2:45pm PPMD also sent out a request to urge people to contact house members with this. Along with a letter to Janet Woodcock

http://community.parentprojectmd.org/profiles/blogs/action-alert-urge-house-member-apply-fdasia-tools-to-duchenne

https://secure2.convio.net/ppmd/site/Advocacy?cmd=display&page=UserAction&id=216

I think a defeat here likely sets DMD drug development back a few years. If the magnitude of efficacy needed will require a 3-5 year trial (just speculating on my part) to show significance BMRN won't and SRPT can't do that.