Silencing Genes For Life™
ddRNAi: expressed RNA interference technology ddRNAi (DNA-directed RNAi) is a unique platform technology for silencing unwanted or disease-causing genes. In the context of therapy, ddRNAi avoids many of the drawbacks of other gene silencing technologies and produces much longer-lasting effects. Benitec Biopharma pioneered ddRNAi and was the first company to demonstrate expressed RNAi in human cells. We hold a dominant intellectual property position in RNAi, with over 40 issued global patents for the human use of ddRNAi. Learn how ddRNAi could target countless human and viral genes. Track our pipeline programs using this exciting technology. View the scope of our patents in ddRNAi. Join us in developing transformational solutions for human health.
Pipeline for ddRNAi gene silencing
Benitec Biopharma’s pipeline of in-house and partnered programs to develop therapeutics for chronic and life-threatening conditions is based on our proprietary technology, DNA-directed RNA(ddRNAi). View our out-licensed programs
Due to its demonstrated ability to effect long-lasting gene silencing, once proven in human trials, ddRNAi technology has significant potential to treat or cure a broad range of human diseases and conditions. These include cancers, neurological diseases, infectious diseases, autoimmune diseases, genetic diseases and other afflictions that are associated with the expression of a small number of key genes.
Our in-house pipeline is summarized below, In-house pipeline
. View our out-licensed programs Out-licensed programs Successful development of therapeutic products in just one of these programs would be a major breakthrough in medical therapy.