JUST IN: $ORTX Orchard Therapeutics Receives Positive CHMP Opinion for Libmeldy(TM) for the Treatment of Early-Onset Metachromatic Leukodystrophy (MLD)
First therapy recommended for full marketing authorization in the EU for eligible patients with confirmed diagnosis of late infantile or early juvenile MLD variants One-time treatment with Libmeldy has been shown to preserve cognitive and motor function in most patients ...
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